1  Synopsis

Protocol number NVT-AD-3001
Study title A 24-week, randomised, double-blind, placebo-controlled study of xanomeline transdermal therapeutic system in patients with mild to moderate Alzheimer's disease
Sponsor Nordvale Therapeutics
Investigational product Xanomeline transdermal therapeutic system (TTS)
Study phase Phase 2
Indication Mild to moderate Alzheimer's disease
Study design Randomised, double-blind, placebo-controlled, three parallel groups
Treatment groups Placebo, xanomeline low dose (50 cm2), xanomeline high dose (75 cm2)
Planned duration of treatment 24 weeks
Primary endpoint Time to first dermatologic treatment-emergent adverse event
Secondary endpoint Change from baseline in systolic blood pressure at week 24
Analysis populations Randomised (intention-to-treat), safety and per-protocol populations
Statistical methods Kaplan-Meier estimation and Cox proportional hazards for the primary endpoint; analysis of covariance for the secondary endpoint

1.1 Subject disposition and key results

A total of 254 subjects were randomised and 254 received at least one dose of study drug. Of these, 110 subjects (43.3%) completed the 24-week treatment period.

At least one treatment-emergent adverse event was reported for 217 subjects (85.4%), and 98 subjects (38.6%) reported at least one dermatologic treatment-emergent adverse event. Dermatologic events occurred earlier and more frequently in both xanomeline groups than in the placebo group, which is consistent with the transdermal route of administration.

No new safety signal was identified beyond the application-site and dermatologic events expected for this formulation.