Appendix A — Listings

A.1 Individual subject data listings

Listing 16.2.1.1: Subjects who discontinued the study. Randomised population.
Subject Treatment Age (years) Sex Treatment duration (days) Reason for discontinuation
01-701-1023 Placebo 64 Male 28 Adverse event
01-701-1047 Placebo 85 Female 26 Adverse event
01-701-1345 Placebo 63 Female 162 Study terminated by sponsor
01-701-1387 Placebo 87 Female 14 Protocol violation
01-703-1096 Placebo 81 Female 51 Lost to follow-up
01-703-1175 Placebo 75 Male 7 Protocol violation
01-704-1010 Placebo 80 Male 138 Withdrawal by subject
01-704-1233 Placebo 87 Female 15 Withdrawal by subject
01-704-1260 Placebo 71 Female 67 Withdrawal by subject
01-704-1435 Placebo 74 Male 54 Withdrawal by subject
01-704-1445 Placebo 75 Male 175 Death
01-705-1018 Placebo 69 Female NA Withdrawal by subject
01-705-1059 Placebo 66 Female 123 Adverse event
01-705-1186 Placebo 84 Female 19 Physician decision
01-708-1158 Placebo 81 Female 42 Adverse event
01-708-1378 Placebo 67 Male 148 Study terminated by sponsor
01-709-1259 Placebo 82 Male 139 Lack of efficacy
01-709-1306 Placebo 60 Female 134 Adverse event
01-710-1083 Placebo 89 Female 11 Death
01-710-1264 Placebo 78 Male 121 Adverse event
01-710-1271 Placebo 86 Female 56 Adverse event
01-710-1314 Placebo 78 Female 30 Withdrawal by subject
01-710-1315 Placebo 83 Female 130 Adverse event
01-715-1155 Placebo 59 Female 44 Withdrawal by subject
01-716-1308 Placebo 76 Female 41 Withdrawal by subject
01-717-1201 Placebo 85 Female 65 Lack of efficacy
01-717-1344 Placebo 64 Female 63 Lack of efficacy
01-718-1172 Placebo 74 Male 70 Withdrawal by subject
01-701-1033 Xanomeline Low Dose 74 Male 14 Study terminated by sponsor
01-701-1111 Xanomeline Low Dose 81 Female 10 Adverse event
01-701-1115 Xanomeline Low Dose 84 Male 55 Adverse event
01-701-1188 Xanomeline Low Dose 71 Male 38 Adverse event
01-701-1211 Xanomeline Low Dose 76 Female 59 Death
01-701-1294 Xanomeline Low Dose 67 Male 83 Adverse event
01-701-1341 Xanomeline Low Dose 51 Male 22 Adverse event
01-701-1429 Xanomeline Low Dose 84 Female 43 Withdrawal by subject
01-702-1082 Xanomeline Low Dose 84 Female 80 Withdrawal by subject
01-703-1086 Xanomeline Low Dose 71 Male 94 Adverse event
01-703-1119 Xanomeline Low Dose 81 Female 114 Adverse event
01-703-1182 Xanomeline Low Dose 84 Male 56 Adverse event
01-703-1197 Xanomeline Low Dose 76 Female 14 Withdrawal by subject
01-703-1279 Xanomeline Low Dose 72 Female 22 Withdrawal by subject
01-704-1009 Xanomeline Low Dose 83 Male 30 Withdrawal by subject
01-704-1025 Xanomeline Low Dose 81 Female 28 Adverse event
01-704-1114 Xanomeline Low Dose 77 Male 166 Withdrawal by subject
01-704-1120 Xanomeline Low Dose 71 Female 62 Adverse event
01-704-1323 Xanomeline Low Dose 68 Female 29 Adverse event
01-704-1325 Xanomeline Low Dose 81 Male 73 Protocol violation
01-705-1031 Xanomeline Low Dose 56 Female 22 Lost to follow-up
01-705-1199 Xanomeline Low Dose 87 Male 13 Adverse event
01-705-1393 Xanomeline Low Dose 84 Female 148 Adverse event
01-706-1384 Xanomeline Low Dose 74 Female 10 Adverse event
01-707-1037 Xanomeline Low Dose 72 Female 5 Withdrawal by subject
01-708-1019 Xanomeline Low Dose 68 Male 13 Adverse event
01-708-1032 Xanomeline Low Dose 62 Male 21 Adverse event
01-708-1272 Xanomeline Low Dose 82 Male 45 Withdrawal by subject
01-708-1297 Xanomeline Low Dose 61 Male 99 Adverse event
01-708-1353 Xanomeline Low Dose 87 Female 56 Adverse event
01-708-1428 Xanomeline Low Dose 84 Female 36 Adverse event
01-709-1007 Xanomeline Low Dose 54 Female 29 Adverse event
01-709-1081 Xanomeline Low Dose 86 Female 100 Adverse event
01-709-1102 Xanomeline Low Dose 71 Female 72 Adverse event
01-709-1217 Xanomeline Low Dose 77 Male 100 Adverse event
01-709-1285 Xanomeline Low Dose 87 Male 61 Study terminated by sponsor
01-710-1002 Xanomeline Low Dose 88 Male 5 Adverse event
01-710-1045 Xanomeline Low Dose 83 Female 72 Adverse event
01-710-1053 Xanomeline Low Dose 84 Female 47 Adverse event
01-710-1154 Xanomeline Low Dose 84 Male 30 Adverse event
01-710-1166 Xanomeline Low Dose 81 Female 110 Adverse event
01-710-1270 Xanomeline Low Dose 83 Female 18 Adverse event
01-710-1300 Xanomeline Low Dose 78 Female 63 Adverse event
01-710-1358 Xanomeline Low Dose 82 Male 146 Withdrawal by subject
01-710-1385 Xanomeline Low Dose 77 Male 113 Adverse event
01-711-1143 Xanomeline Low Dose 76 Female 58 Adverse event
01-713-1448 Xanomeline Low Dose 71 Female 118 Adverse event
01-714-1068 Xanomeline Low Dose 79 Female 62 Adverse event
01-715-1107 Xanomeline Low Dose 65 Male 71 Adverse event
01-715-1405 Xanomeline Low Dose 69 Male 2 Adverse event
01-716-1063 Xanomeline Low Dose 80 Male 109 Adverse event
01-716-1094 Xanomeline Low Dose 82 Male 37 Adverse event
01-716-1151 Xanomeline Low Dose 83 Female 100 Adverse event
01-716-1298 Xanomeline Low Dose 76 Female 82 Adverse event
01-716-1311 Xanomeline Low Dose 78 Male 131 Withdrawal by subject
01-718-1066 Xanomeline Low Dose 79 Female 10 Adverse event
01-718-1079 Xanomeline Low Dose 67 Female 43 Adverse event
01-718-1170 Xanomeline Low Dose 80 Female 27 Adverse event
01-718-1250 Xanomeline Low Dose 82 Female 133 Adverse event
01-701-1146 Xanomeline High Dose 75 Female 38 Adverse event
01-701-1180 Xanomeline High Dose 56 Male 35 Adverse event
01-701-1181 Xanomeline High Dose 79 Female 5 Adverse event
01-701-1275 Xanomeline High Dose 61 Male 114 Withdrawal by subject
01-701-1302 Xanomeline High Dose 61 Male 69 Adverse event
01-701-1360 Xanomeline High Dose 67 Male 6 Physician decision
01-701-1444 Xanomeline High Dose 63 Male 39 Adverse event
01-703-1076 Xanomeline High Dose 69 Male 61 Adverse event
01-703-1258 Xanomeline High Dose 78 Female 176 Adverse event
01-703-1295 Xanomeline High Dose 88 Female 150 Withdrawal by subject
01-703-1335 Xanomeline High Dose 67 Female 52 Protocol violation
01-703-1403 Xanomeline High Dose 67 Male 2 Adverse event
01-704-1008 Xanomeline High Dose 76 Female 40 Adverse event
01-704-1017 Xanomeline High Dose 77 Male 44 Adverse event
01-704-1065 Xanomeline High Dose 75 Male 60 Adverse event
01-704-1074 Xanomeline High Dose 80 Female 58 Adverse event
01-704-1093 Xanomeline High Dose 79 Male 95 Adverse event
01-704-1241 Xanomeline High Dose 86 Male 46 Adverse event
01-704-1266 Xanomeline High Dose 82 Male 55 Adverse event
01-704-1332 Xanomeline High Dose 80 Male 68 Adverse event
01-705-1281 Xanomeline High Dose 73 Female 92 Adverse event
01-705-1303 Xanomeline High Dose 72 Male 15 Adverse event
01-705-1310 Xanomeline High Dose 74 Female 83 Adverse event
01-705-1377 Xanomeline High Dose 63 Female 22 Withdrawal by subject
01-705-1382 Xanomeline High Dose 82 Male NA Protocol violation
01-706-1049 Xanomeline High Dose 60 Female 36 Adverse event
01-708-1178 Xanomeline High Dose 77 Female 99 Physician decision
01-708-1213 Xanomeline High Dose 76 Female 14 Adverse event
01-708-1216 Xanomeline High Dose 78 Male 37 Adverse event
01-708-1236 Xanomeline High Dose 86 Female 1 Withdrawal by subject
01-708-1347 Xanomeline High Dose 61 Female 60 Adverse event
01-708-1372 Xanomeline High Dose 84 Male 8 Protocol violation
01-709-1168 Xanomeline High Dose 72 Female 56 Adverse event
01-709-1238 Xanomeline High Dose 69 Male 84 Adverse event
01-709-1329 Xanomeline High Dose 70 Male 11 Withdrawal by subject
01-709-1424 Xanomeline High Dose 77 Male 5 Adverse event
01-710-1021 Xanomeline High Dose 79 Male 33 Adverse event
01-710-1070 Xanomeline High Dose 85 Female 137 Adverse event
01-710-1137 Xanomeline High Dose 79 Female 34 Adverse event
01-710-1142 Xanomeline High Dose 76 Female 19 Adverse event
01-710-1278 Xanomeline High Dose 81 Male 65 Adverse event
01-711-1012 Xanomeline High Dose 67 Female 27 Adverse event
01-711-1433 Xanomeline High Dose 84 Female 10 Adverse event
01-713-1141 Xanomeline High Dose 79 Male 32 Adverse event
01-714-1425 Xanomeline High Dose 81 Male 5 Study terminated by sponsor
01-715-1319 Xanomeline High Dose 65 Male 17 Withdrawal by subject
01-715-1321 Xanomeline High Dose 75 Female 70 Adverse event
01-716-1030 Xanomeline High Dose 83 Female 6 Withdrawal by subject
01-716-1071 Xanomeline High Dose 78 Female 55 Adverse event
01-716-1189 Xanomeline High Dose 81 Male 142 Adverse event
01-716-1229 Xanomeline High Dose 73 Female 40 Adverse event
01-716-1373 Xanomeline High Dose 74 Male 76 Adverse event
01-717-1357 Xanomeline High Dose 77 Male 167 Study terminated by sponsor
01-718-1101 Xanomeline High Dose 82 Male 165 Study terminated by sponsor
01-718-1328 Xanomeline High Dose 86 Male 77 Withdrawal by subject
01-718-1371 Xanomeline High Dose 69 Female 98 Adverse event
01-718-1427 Xanomeline High Dose 74 Female 57 Lack of efficacy
One row per subject. Reasons come from the disposition domain.
Listing 16.2.2.1: Subjects who discontinued for a protocol violation. Randomised population.
Subject Treatment Age (years) Sex Treatment duration (days) End of study status
01-701-1387 Placebo 87 Female 14 Discontinued
01-703-1175 Placebo 75 Male 7 Discontinued
01-704-1325 Xanomeline Low Dose 81 Male 73 Discontinued
01-703-1335 Xanomeline High Dose 67 Female 52 Discontinued
01-705-1382 Xanomeline High Dose 82 Male NA Discontinued
01-708-1372 Xanomeline High Dose 84 Male 8 Discontinued
The pilot study ships no protocol deviation dataset, so this listing covers only violations severe enough to end study participation. Deviations that did not lead to discontinuation cannot be listed.
Listing 16.2.4.1: Demographic data. Randomised population.
Subject Treatment Age (years) Age group Sex Race Completed
01-701-1015 Placebo 63 18-64 Female White Yes
01-701-1023 Placebo 64 18-64 Male White No
01-701-1047 Placebo 85 >64 Female White No
01-701-1118 Placebo 52 18-64 Male White Yes
01-701-1130 Placebo 84 >64 Male White Yes
01-701-1153 Placebo 79 >64 Female White Yes
01-701-1203 Placebo 81 >64 Female Black or african american Yes
01-701-1234 Placebo 69 >64 Male White Yes
01-701-1345 Placebo 63 18-64 Female White No
01-701-1363 Placebo 81 >64 Female Black or african american Yes
01-701-1387 Placebo 87 >64 Female White No
01-701-1392 Placebo 78 >64 Male White Yes
01-701-1415 Placebo 85 >64 Male White Yes
01-701-1440 Placebo 70 >64 Male White Yes
01-703-1042 Placebo 64 18-64 Male White Yes
01-703-1096 Placebo 81 >64 Female White No
01-703-1100 Placebo 84 >64 Female White Yes
01-703-1175 Placebo 75 >64 Male White No
01-703-1210 Placebo 72 >64 Female White Yes
01-703-1299 Placebo 81 >64 Female White Yes
01-704-1010 Placebo 80 >64 Male White No
01-704-1127 Placebo 84 >64 Female White Yes
01-704-1164 Placebo 67 >64 Female White Yes
01-704-1233 Placebo 87 >64 Female White No
01-704-1260 Placebo 71 >64 Female White No
01-704-1351 Placebo 70 >64 Male White Yes
01-704-1388 Placebo 81 >64 Male White Yes
01-704-1435 Placebo 74 >64 Male White No
01-704-1445 Placebo 75 >64 Male White No
01-705-1018 Placebo 69 >64 Female White No
01-705-1059 Placebo 66 >64 Female White No
01-705-1186 Placebo 84 >64 Female White No
01-705-1282 Placebo 70 >64 Female Black or african american Yes
01-705-1349 Placebo 86 >64 Female White Yes
01-706-1041 Placebo 64 18-64 Female Black or african american Yes
01-707-1206 Placebo 65 >64 Male White Yes
01-708-1087 Placebo 74 >64 Female White Yes
01-708-1158 Placebo 81 >64 Female White No
01-708-1171 Placebo 77 >64 Female White Yes
01-708-1253 Placebo 61 18-64 Male White Yes
01-708-1286 Placebo 80 >64 Female Black or african american Yes
01-708-1296 Placebo 57 18-64 Male Black or african american Yes
01-708-1316 Placebo 74 >64 Female White Yes
01-708-1342 Placebo 59 18-64 Female White Yes
01-708-1378 Placebo 67 >64 Male Black or african american No
01-709-1001 Placebo 76 >64 Female White Yes
01-709-1088 Placebo 69 >64 Male White Yes
01-709-1259 Placebo 82 >64 Male White No
01-709-1301 Placebo 62 18-64 Female White Yes
01-709-1306 Placebo 60 18-64 Female White No
01-709-1312 Placebo 68 >64 Female White Yes
01-709-1339 Placebo 81 >64 Male White Yes
01-710-1027 Placebo 83 >64 Male White Yes
01-710-1060 Placebo 82 >64 Male White Yes
01-710-1077 Placebo 76 >64 Female White Yes
01-710-1078 Placebo 81 >64 Female White Yes
01-710-1083 Placebo 89 >64 Female White No
01-710-1183 Placebo 80 >64 Female White Yes
01-710-1264 Placebo 78 >64 Male White No
01-710-1271 Placebo 86 >64 Female White No
01-710-1314 Placebo 78 >64 Female White No
01-710-1315 Placebo 83 >64 Female White No
01-710-1368 Placebo 88 >64 Female White Yes
01-711-1036 Placebo 70 >64 Male Black or african american Yes
01-713-1179 Placebo 64 18-64 Female White Yes
01-713-1256 Placebo 71 >64 Male White Yes
01-713-1269 Placebo 73 >64 Male White Yes
01-714-1035 Placebo 88 >64 Female White Yes
01-714-1375 Placebo 78 >64 Female White Yes
01-715-1155 Placebo 59 18-64 Female White No
01-715-1207 Placebo 78 >64 Female White Yes
01-715-1397 Placebo 76 >64 Female White Yes
01-716-1024 Placebo 87 >64 Female White Yes
01-716-1026 Placebo 73 >64 Female White Yes
01-716-1044 Placebo 74 >64 Male White Yes
01-716-1108 Placebo 86 >64 Female White Yes
01-716-1160 Placebo 83 >64 Female White Yes
01-716-1177 Placebo 72 >64 Male White Yes
01-716-1308 Placebo 76 >64 Female White No
01-716-1441 Placebo 85 >64 Male White Yes
01-717-1201 Placebo 85 >64 Female White No
01-717-1344 Placebo 64 18-64 Female White No
01-718-1139 Placebo 77 >64 Male White Yes
01-718-1150 Placebo 73 >64 Female White Yes
01-718-1172 Placebo 74 >64 Male White No
01-718-1355 Placebo 79 >64 Male White Yes
01-701-1033 Xanomeline Low Dose 74 >64 Male White No
01-701-1097 Xanomeline Low Dose 68 >64 Male White Yes
01-701-1111 Xanomeline Low Dose 81 >64 Female White No
01-701-1115 Xanomeline Low Dose 84 >64 Male White No
01-701-1188 Xanomeline Low Dose 71 >64 Male White No
01-701-1192 Xanomeline Low Dose 80 >64 Female White Yes
01-701-1211 Xanomeline Low Dose 76 >64 Female White No
01-701-1294 Xanomeline Low Dose 67 >64 Male White No
01-701-1317 Xanomeline Low Dose 68 >64 Male White Yes
01-701-1324 Xanomeline Low Dose 79 >64 Male White Yes
01-701-1341 Xanomeline Low Dose 51 18-64 Male White No
01-701-1429 Xanomeline Low Dose 84 >64 Female White No
01-701-1442 Xanomeline Low Dose 57 18-64 Female Black or african american Yes
01-702-1082 Xanomeline Low Dose 84 >64 Female White No
01-703-1086 Xanomeline Low Dose 71 >64 Male White No
01-703-1119 Xanomeline Low Dose 81 >64 Female White No
01-703-1182 Xanomeline Low Dose 84 >64 Male White No
01-703-1197 Xanomeline Low Dose 76 >64 Female Black or african american No
01-703-1279 Xanomeline Low Dose 72 >64 Female White No
01-703-1379 Xanomeline Low Dose 81 >64 Female Black or african american Yes
01-704-1009 Xanomeline Low Dose 83 >64 Male White No
01-704-1025 Xanomeline Low Dose 81 >64 Female White No
01-704-1114 Xanomeline Low Dose 77 >64 Male White No
01-704-1120 Xanomeline Low Dose 71 >64 Female White No
01-704-1135 Xanomeline Low Dose 74 >64 Female White Yes
01-704-1218 Xanomeline Low Dose 81 >64 Female White Yes
01-704-1323 Xanomeline Low Dose 68 >64 Female White No
01-704-1325 Xanomeline Low Dose 81 >64 Male White No
01-705-1031 Xanomeline Low Dose 56 18-64 Female White No
01-705-1199 Xanomeline Low Dose 87 >64 Male White No
01-705-1292 Xanomeline Low Dose 60 18-64 Female Black or african american Yes
01-705-1393 Xanomeline Low Dose 84 >64 Female White No
01-705-1431 Xanomeline Low Dose 68 >64 Female White Yes
01-706-1384 Xanomeline Low Dose 74 >64 Female White No
01-707-1037 Xanomeline Low Dose 72 >64 Female White No
01-708-1019 Xanomeline Low Dose 68 >64 Male White No
01-708-1032 Xanomeline Low Dose 62 18-64 Male White No
01-708-1084 Xanomeline Low Dose 73 >64 Female White Yes
01-708-1272 Xanomeline Low Dose 82 >64 Male White No
01-708-1297 Xanomeline Low Dose 61 18-64 Male White No
01-708-1348 Xanomeline Low Dose 79 >64 Female White Yes
01-708-1353 Xanomeline Low Dose 87 >64 Female Black or african american No
01-708-1428 Xanomeline Low Dose 84 >64 Female White No
01-709-1007 Xanomeline Low Dose 54 18-64 Female White No
01-709-1020 Xanomeline Low Dose 72 >64 Female White Yes
01-709-1081 Xanomeline Low Dose 86 >64 Female White No
01-709-1102 Xanomeline Low Dose 71 >64 Female White No
01-709-1217 Xanomeline Low Dose 77 >64 Male White No
01-709-1285 Xanomeline Low Dose 87 >64 Male White No
01-709-1326 Xanomeline Low Dose 75 >64 Female White Yes
01-710-1002 Xanomeline Low Dose 88 >64 Male White No
01-710-1045 Xanomeline Low Dose 83 >64 Female White No
01-710-1053 Xanomeline Low Dose 84 >64 Female White No
01-710-1154 Xanomeline Low Dose 84 >64 Male White No
01-710-1166 Xanomeline Low Dose 81 >64 Female White No
01-710-1235 Xanomeline Low Dose 56 18-64 Female White Yes
01-710-1270 Xanomeline Low Dose 83 >64 Female White No
01-710-1300 Xanomeline Low Dose 78 >64 Female White No
01-710-1358 Xanomeline Low Dose 82 >64 Male White No
01-710-1385 Xanomeline Low Dose 77 >64 Male White No
01-711-1143 Xanomeline Low Dose 76 >64 Female White No
01-713-1043 Xanomeline Low Dose 78 >64 Female White Yes
01-713-1073 Xanomeline Low Dose 74 >64 Female Black or african american Yes
01-713-1448 Xanomeline Low Dose 71 >64 Female White No
01-714-1068 Xanomeline Low Dose 79 >64 Female White No
01-714-1195 Xanomeline Low Dose 75 >64 Male White Yes
01-715-1085 Xanomeline Low Dose 77 >64 Female White Yes
01-715-1107 Xanomeline Low Dose 65 >64 Male White No
01-715-1405 Xanomeline Low Dose 69 >64 Male White No
01-716-1063 Xanomeline Low Dose 80 >64 Male White No
01-716-1094 Xanomeline Low Dose 82 >64 Male White No
01-716-1103 Xanomeline Low Dose 79 >64 Male White Yes
01-716-1151 Xanomeline Low Dose 83 >64 Female White No
01-716-1157 Xanomeline Low Dose 85 >64 Male White Yes
01-716-1167 Xanomeline Low Dose 68 >64 Male White Yes
01-716-1298 Xanomeline Low Dose 76 >64 Female White No
01-716-1311 Xanomeline Low Dose 78 >64 Male White No
01-717-1004 Xanomeline Low Dose 80 >64 Female White Yes
01-717-1446 Xanomeline Low Dose 75 >64 Female White Yes
01-718-1066 Xanomeline Low Dose 79 >64 Female White No
01-718-1079 Xanomeline Low Dose 67 >64 Female White No
01-718-1170 Xanomeline Low Dose 80 >64 Female White No
01-718-1250 Xanomeline Low Dose 82 >64 Female White No
01-718-1254 Xanomeline Low Dose 78 >64 Male White Yes
01-701-1028 Xanomeline High Dose 71 >64 Male White Yes
01-701-1034 Xanomeline High Dose 77 >64 Female White Yes
01-701-1133 Xanomeline High Dose 81 >64 Female White Yes
01-701-1146 Xanomeline High Dose 75 >64 Female White No
01-701-1148 Xanomeline High Dose 57 18-64 Male White Yes
01-701-1180 Xanomeline High Dose 56 18-64 Male White No
01-701-1181 Xanomeline High Dose 79 >64 Female White No
01-701-1239 Xanomeline High Dose 56 18-64 Male White Yes
01-701-1275 Xanomeline High Dose 61 18-64 Male American indian or alaska native No
01-701-1287 Xanomeline High Dose 56 18-64 Female White Yes
01-701-1302 Xanomeline High Dose 61 18-64 Male White No
01-701-1360 Xanomeline High Dose 67 >64 Male White No
01-701-1383 Xanomeline High Dose 72 >64 Female White Yes
01-701-1444 Xanomeline High Dose 63 18-64 Male White No
01-703-1076 Xanomeline High Dose 69 >64 Male White No
01-703-1258 Xanomeline High Dose 78 >64 Female White No
01-703-1295 Xanomeline High Dose 88 >64 Female White No
01-703-1335 Xanomeline High Dose 67 >64 Female Black or african american No
01-703-1403 Xanomeline High Dose 67 >64 Male White No
01-703-1439 Xanomeline High Dose 76 >64 Female White Yes
01-704-1008 Xanomeline High Dose 76 >64 Female White No
01-704-1017 Xanomeline High Dose 77 >64 Male White No
01-704-1065 Xanomeline High Dose 75 >64 Male White No
01-704-1074 Xanomeline High Dose 80 >64 Female White No
01-704-1093 Xanomeline High Dose 79 >64 Male White No
01-704-1241 Xanomeline High Dose 86 >64 Male White No
01-704-1266 Xanomeline High Dose 82 >64 Male White No
01-704-1332 Xanomeline High Dose 80 >64 Male White No
01-705-1280 Xanomeline High Dose 56 18-64 Female White Yes
01-705-1281 Xanomeline High Dose 73 >64 Female Black or african american No
01-705-1303 Xanomeline High Dose 72 >64 Male White No
01-705-1310 Xanomeline High Dose 74 >64 Female White No
01-705-1377 Xanomeline High Dose 63 18-64 Female Black or african american No
01-705-1382 Xanomeline High Dose 82 >64 Male White No
01-706-1049 Xanomeline High Dose 60 18-64 Female White No
01-708-1178 Xanomeline High Dose 77 >64 Female Black or african american No
01-708-1213 Xanomeline High Dose 76 >64 Female White No
01-708-1216 Xanomeline High Dose 78 >64 Male White No
01-708-1236 Xanomeline High Dose 86 >64 Female White No
01-708-1336 Xanomeline High Dose 73 >64 Male White Yes
01-708-1347 Xanomeline High Dose 61 18-64 Female White No
01-708-1372 Xanomeline High Dose 84 >64 Male White No
01-708-1406 Xanomeline High Dose 71 >64 Female White Yes
01-709-1029 Xanomeline High Dose 82 >64 Male White Yes
01-709-1099 Xanomeline High Dose 79 >64 Female White Yes
01-709-1168 Xanomeline High Dose 72 >64 Female White No
01-709-1238 Xanomeline High Dose 69 >64 Male White No
01-709-1309 Xanomeline High Dose 65 >64 Male White Yes
01-709-1329 Xanomeline High Dose 70 >64 Male White No
01-709-1424 Xanomeline High Dose 77 >64 Male White No
01-710-1006 Xanomeline High Dose 77 >64 Male White Yes
01-710-1021 Xanomeline High Dose 79 >64 Male Black or african american No
01-710-1070 Xanomeline High Dose 85 >64 Female White No
01-710-1137 Xanomeline High Dose 79 >64 Female Black or african american No
01-710-1142 Xanomeline High Dose 76 >64 Female White No
01-710-1187 Xanomeline High Dose 78 >64 Female White Yes
01-710-1249 Xanomeline High Dose 79 >64 Male White Yes
01-710-1278 Xanomeline High Dose 81 >64 Male White No
01-710-1354 Xanomeline High Dose 73 >64 Male White Yes
01-710-1408 Xanomeline High Dose 80 >64 Male White Yes
01-711-1012 Xanomeline High Dose 67 >64 Female White No
01-711-1433 Xanomeline High Dose 84 >64 Female White No
01-713-1106 Xanomeline High Dose 74 >64 Male White Yes
01-713-1141 Xanomeline High Dose 79 >64 Male White No
01-713-1209 Xanomeline High Dose 77 >64 Female White Yes
01-714-1288 Xanomeline High Dose 77 >64 Male Black or african american Yes
01-714-1425 Xanomeline High Dose 81 >64 Male White No
01-715-1319 Xanomeline High Dose 65 >64 Male White No
01-715-1321 Xanomeline High Dose 75 >64 Female White No
01-716-1030 Xanomeline High Dose 83 >64 Female White No
01-716-1071 Xanomeline High Dose 78 >64 Female White No
01-716-1189 Xanomeline High Dose 81 >64 Male White No
01-716-1229 Xanomeline High Dose 73 >64 Female White No
01-716-1364 Xanomeline High Dose 84 >64 Female White Yes
01-716-1373 Xanomeline High Dose 74 >64 Male White No
01-716-1418 Xanomeline High Dose 80 >64 Female White Yes
01-716-1447 Xanomeline High Dose 72 >64 Female White Yes
01-717-1109 Xanomeline High Dose 84 >64 Male White Yes
01-717-1174 Xanomeline High Dose 73 >64 Male White Yes
01-717-1357 Xanomeline High Dose 77 >64 Male White No
01-718-1101 Xanomeline High Dose 82 >64 Male Black or african american No
01-718-1328 Xanomeline High Dose 86 >64 Male White No
01-718-1371 Xanomeline High Dose 69 >64 Female White No
01-718-1427 Xanomeline High Dose 74 >64 Female Black or african american No
One row per subject, in treatment group and subject identifier order.
Listing 16.2.7.1: Serious treatment-emergent adverse events. Safety population.
Subject Treatment Preferred term System organ class Onset day Severity Related Outcome
01-709-1424 Xanomeline Low Dose Syncope Nervous system disorders 5 Moderate Yes Recovered/resolved
01-718-1170 Xanomeline Low Dose Syncope Nervous system disorders 27 Severe Yes Recovered/resolved
01-718-1371 Xanomeline High Dose Partial seizures with secondary generalisation Nervous system disorders 38 Severe No Recovered/resolved
Onset day is relative to the first dose of study drug. One row per event.
Listing 16.2.8.1: Abnormal laboratory values meeting a liver-injury criterion. Safety population.
Subject Treatment Analyte Visit Worst post-baseline value Upper limit of reference range Multiple of upper limit
01-705-1186 Placebo Alanine Aminotransferase (U/L) Week 4 107.0 32.0 3.3
01-705-1186 Placebo Aspartate Aminotransferase (U/L) Week 4 135.0 34.0 4.0
01-705-1186 Placebo Bilirubin (umol/L) Unscheduled 4.1 124.8 21.0 5.9
01-708-1286 Placebo Alanine Aminotransferase (U/L) Week 24 124.0 32.0 3.9
01-708-1286 Placebo Aspartate Aminotransferase (U/L) Week 24 168.0 34.0 4.9
01-708-1286 Placebo Bilirubin (umol/L) Week 16 8.5 21.0 0.4
01-705-1292 Xanomeline Low Dose Alanine Aminotransferase (U/L) Week 12 88.0 34.0 2.6
01-705-1292 Xanomeline Low Dose Aspartate Aminotransferase (U/L) Week 12 125.0 34.0 3.7
01-705-1292 Xanomeline Low Dose Bilirubin (umol/L) Week 24 12.0 21.0 0.6
01-705-1310 Xanomeline High Dose Alanine Aminotransferase (U/L) Week 8 129.0 32.0 4.0
01-705-1310 Xanomeline High Dose Aspartate Aminotransferase (U/L) Week 8 114.0 34.0 3.4
01-705-1310 Xanomeline High Dose Bilirubin (umol/L) Week 8 15.4 21.0 0.7
01-709-1029 Xanomeline High Dose Alanine Aminotransferase (U/L) Week 26 18.0 35.0 0.5
01-709-1029 Xanomeline High Dose Aspartate Aminotransferase (U/L) Week 24 27.0 36.0 0.8
01-709-1029 Xanomeline High Dose Bilirubin (umol/L) Week 20 53.0 21.0 2.5
One row per subject per analyte, showing the worst post-baseline value and its multiple of the upper limit of the reference range. Restricted to the analytes screened in the potential drug-induced liver injury table.

A.2 Index of outputs

Every table, figure and listing of this report carries the ICH E3 output number that R/tlf-index.R holds for it. The index below lists them all, with the ICH E3 section each number belongs to and the population the output was computed on.

Table 14.1.1

Analysis populations. ICH E3 section 14.1. Randomised population.

Table 14.1.2

Subject disposition. ICH E3 section 14.1. Randomised population.

Table 14.1.3

Demographic and baseline characteristics. ICH E3 section 14.1. Randomised population.

Table 14.1.4

Medical history by body system and preferred term. ICH E3 section 14.1. Conditions reported by at least 5% of subjects in any treatment group, randomised population.

Figure 14.1.1

Disposition of subjects from screening to study completion (Schulz et al. 2010). ICH E3 section 14.1.

Table 14.2.1

Time to first dermatologic treatment-emergent adverse event. ICH E3 section 14.2. Intention-to-treat population.

Table 14.2.1.1

Time to first dermatologic treatment-emergent adverse event (supportive analysis). ICH E3 section 14.2. Per-protocol population.

Table 14.2.2

Change from baseline in supine systolic blood pressure at week 24. ICH E3 section 14.2. Safety population.

Figure 14.2.1

Cumulative incidence of the first dermatologic treatment-emergent adverse event, intention-to-treat population. ICH E3 section 14.2.

Figure 14.2.2

Hazard ratio for the primary endpoint by age group and sex, intention-to-treat population. ICH E3 section 14.2.

Figure 14.2.3

Mean supine systolic blood pressure by visit and treatment group, safety population. ICH E3 section 14.2.

Table 14.3.5

Extent of exposure. ICH E3 section 14.3. Safety population.

Table 14.3.6

Prior and concomitant medications by drug class and preferred term. ICH E3 section 14.3. Medications taken by at least 5% of subjects in any treatment group, safety population.

Table 14.3.1.1

Overview of treatment-emergent adverse events. ICH E3 section 14.3.1. Safety population.

Table 14.3.1.2

Treatment-emergent adverse events by system organ class and preferred term. ICH E3 section 14.3.1. Events reported by at least 5% of subjects in any treatment group, safety population.

Table 14.3.1.3

Treatment-emergent adverse events by maximum severity. ICH E3 section 14.3.1. Events reported by at least 5% of subjects in any treatment group, safety population.

Table 14.3.1.4

Treatment-emergent adverse events by relationship to study drug. ICH E3 section 14.3.1. Events reported by at least 5% of subjects in any treatment group, safety population.

Table 14.3.1.5

Serious treatment-emergent adverse events. ICH E3 section 14.3.1. Safety population.

Table 14.3.4.1

Shift from baseline to worst post-baseline category. ICH E3 section 14.3.4. Alanine aminotransferase, safety population.

Table 14.3.4.2

Shift from baseline to worst post-baseline category. ICH E3 section 14.3.4. Aspartate aminotransferase, safety population.

Table 14.3.4.3

Shift from baseline to worst post-baseline category. ICH E3 section 14.3.4. Bilirubin, safety population.

Table 14.3.4.4

Shift from baseline to worst post-baseline category. ICH E3 section 14.3.4. Creatinine, safety population.

Table 14.3.4.5

Potential drug-induced liver injury. ICH E3 section 14.3.4. Safety population.

Table 14.3.7

Shift from baseline to worst post-baseline category. ICH E3 section 14.3. Systolic blood pressure measured supine, safety population.

Table 14.3.8

Shift from baseline to worst post-baseline category. ICH E3 section 14.3. QTcF interval, safety population.

Listing 16.2.1.1

Subjects who discontinued the study. ICH E3 section 16.2.1. Randomised population.

Listing 16.2.2.1

Subjects who discontinued for a protocol violation. ICH E3 section 16.2.2. Randomised population.

Listing 16.2.4.1

Demographic data. ICH E3 section 16.2.4. Randomised population.

Listing 16.2.7.1

Serious treatment-emergent adverse events. ICH E3 section 16.2.7. Safety population.

Listing 16.2.8.1

Abnormal laboratory values meeting a liver-injury criterion. ICH E3 section 16.2.8. Safety population.